Poster Presentation Clinical Oncology Society of Australia Annual Scientific Meeting 2026

Ionizable Lipids Discovery Enable Functional mRNA Delivery for Clinical Translation of mRNA Vaccines (146263)

Wen-Shan Li 1 , Jhih-Liang Huang 1 , Hsing-Pang Hsieh 2 , Han-Chung Wu 3
  1. Institute of Chemistry, Academia Sinica, Taipei, Taiwan
  2. Institute of Biotech and Pharma Research, National Health Research Institutes, Miaoli County, Taiwan
  3. Institute of Cellular and Organismic Biology, Academia Sinica, Taipei, Taiwan

LNP-based technology protects and delivers mRNA into cells, but optimizing stability, reducing side effects, and ensuring equitable global distribution remain critical unmet clinical needs [1]. For these purposes, we discover a new series of malonate-based ionizable lipids for intramuscular mRNA delivery. A 1.5- to 3-fold increase in translation efficiency was observed when mRNA was delivered via malonate lipids AS-CL05 and AS-CL09, significantly outperforming vehicles MC3 and SM102. Furthermore, structural optimization of these lipids significantly enhanced mRNA delivery efficiency. Specifically, lipid nanoparticle (LNP) formulations based on lipid AS-CL28, encapsulating wild-type firefly luciferase (FLS-WT) mRNA, exhibited a two-fold increase in neutralizing capacity compared to lipid AS-CL09. Concurrently, lipid AS-CL29-based LNPs encapsulating dengue virus serotype 2 envelope (DENV2 E) mRNA demonstrated superior potency, yielding a 50% plaque reduction neutralization test PRNT50 titer of 7,211, which surpassed the efficacy of both lipids AS-CL28- and AS-CL09-based formulations [2]. In conclusion, these findings highlight the utility of malonate-based lipids for mRNA delivery, establishing their versatility across a diverse range of mRNA payloads.

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